Steroid Metabolism, Inborn Errors: Clinical Trials

2 trials for Steroid Metabolism, Inborn Errors, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

2 terminated. 2 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 12Terminated 2

Follow Steroid Metabolism, Inborn Errors: new trials by email Literature Review of Steroid Metabolism, Inborn Errors trials Research Report on Steroid Metabolism, Inborn Errors

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Neoadjuvant ADI-PEG 20 + Ifosfamide + Radiotherapy in Soft Tissue Sarcoma
ADI PEG20, Ifosfamide, Radiotherapy - Soft Tissue Sarcoma, Sts
Phase 1TerminatedWashington University School of Medicine62024-03-142026-09-03
Androgen Reduction in Congenital Adrenal Hyperplasia, Phase 1
Abiraterone acetate - Congenital Adrenal Hyperplasia
Phase 1TerminatedUniversity of Texas Southwestern Medical Center42017-08-012025-11-04

Narrower conditions

Adrenal Hyperplasia, Congenital (1)  ·  Ichthyosis, X-Linked (1)  ·  Sarcoma (1)

Broader conditions

Congenital Abnormalities (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Genetic Diseases, Inborn (2)  ·  Metabolic Diseases (2)  ·  Metabolism, Inborn Errors (2)  ·  Nutritional and Metabolic Diseases (2)  ·  Adrenal Gland Diseases (1)  ·  Adrenogenital Syndrome (1)  ·  Disorders of Sex Development (1)  ·  Endocrine System Diseases (1)  ·  Female Urogenital Diseases (1)  ·  Female Urogenital Diseases and Pregnancy Complications (1)  ·  Genetic Diseases, X-Linked (1)  ·  Gonadal Disorders (1)

Interventions

ADI PEG20 (1)  ·  Abiraterone Acetate (1)  ·  Ifosfamide (1)  ·  Mesna (1)  ·  Radiotherapy (1)

Sponsors

University of Texas Southwestern Medical Center (1)  ·  Washington University School of Medicine (1)

Countries

United States (2)

Top investigators

Mia Weiss, M.D. (1)  ·  Perrin C White, MD (1)

NIH funding

U01HD083493 (1)