1 completed, 1 recruiting. 2 Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 2 | Completed 1, Recruiting 1 |
Follow Pyruvate Metabolism, Inborn Errors: new trials by email Literature Review of Pyruvate Metabolism, Inborn Errors trials Research Report on Pyruvate Metabolism, Inborn Errors
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Triheptanoin for Children With Primary-Specific Pyruvate Dehydrogenase Complex (PDC) Deficiency Triheptanoin - Pyruvate Dehydrogenase Complex Deficiency | Phase 1 | Recruiting | Jirair Krikor Bedoyan | 6 | 2024-07-11 | 2026-02-17 |
| A Dose-escalating Clinical Trial With KH176 KH176, placebo - MELAS, LHON | Phase 1 | Completed | Khondrion BV | 32 | 2015-05-01 | 2021-10-18 |
Leigh Disease (1) · MELAS Syndrome (1) · Mitochondrial Diseases (1) · Pyruvate Dehydrogenase Complex Deficiency Disease (1)
Brain Diseases (2) · Brain Diseases, Metabolic (2) · Brain Diseases, Metabolic, Inborn (2) · Carbohydrate Metabolism, Inborn Errors (2) · Central Nervous System Diseases (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Genetic Diseases, Inborn (2) · Metabolic Diseases (2) · Metabolism, Inborn Errors (2) · Nervous System Diseases (2) · Nutritional and Metabolic Diseases (2) · Cardiovascular Diseases (1) · Cerebral Small Vessel Diseases (1) · Cerebrovascular Disorders (1)
6-hydroxy-2,5,7,8-tetramethylchroman-2-carboxylic acid (1) · triheptanoin (1)
Jirair Krikor Bedoyan (1) · Khondrion BV (1)
Belgium (1) · United States (1)