1 active not recruiting. 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 3 | 1 | Active not recruiting 1 |
Follow Pyruvate Dehydrogenase Complex Deficiency Disease: new trials by email Literature Review of Pyruvate Dehydrogenase Complex Deficiency Disease trials Research Report on Pyruvate Dehydrogenase Complex Deficiency Disease
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Trial of Dichloroacetate in Pyruvate Dehydrogenase Complex Deficiency: Dichloroacetate (DCA), Placebo, Genotype - Pyruvate Dehydrogenase Complex Deficiency | Phase 3 | Active not recruiting | Saol Therapeutics Inc | 34 | 2020-07-14 | 2025-05-04 |
Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Carbohydrate Metabolism, Inborn Errors (1) · Central Nervous System Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Genetic Diseases, X-Linked (1) · Heredodegenerative Disorders, Nervous System (1) · Intellectual Disability (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1) · Mitochondrial Diseases (1) · Nervous System Diseases (1) · Neurobehavioral Manifestations (1)
Dichloroacetic Acid (1) · Genotype (1)
United States (1)