1 recruiting. 1 Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Recruiting 1 |
Follow Pyruvate Dehydrogenase Complex Deficiency: new trials by email Literature Review of Pyruvate Dehydrogenase Complex Deficiency trials Research Report on Pyruvate Dehydrogenase Complex Deficiency
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Triheptanoin for Children With Primary-Specific Pyruvate Dehydrogenase Complex (PDC) Deficiency Triheptanoin - Pyruvate Dehydrogenase Complex Deficiency | Phase 1 | Recruiting | Jirair Krikor Bedoyan | 6 | 2024-07-11 | 2026-02-17 |
Pyruvate Dehydrogenase Complex Deficiency Disease (1)
Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Carbohydrate Metabolism, Inborn Errors (1) · Central Nervous System Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Genetic Diseases, X-Linked (1) · Heredodegenerative Disorders, Nervous System (1) · Intellectual Disability (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1) · Mitochondrial Diseases (1) · Nervous System Diseases (1) · Neurobehavioral Manifestations (1)
triheptanoin (1)
United States (1)