Pseudoxanthoma Elasticum: Clinical Trials

2 trials for Pseudoxanthoma Elasticum, newest first

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2 completed. 2 Phase 1, 2 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 12Completed 2
Phase 22Completed 2

Follow Pseudoxanthoma Elasticum: new trials by email Literature Review of Pseudoxanthoma Elasticum trials Research Report on Pseudoxanthoma Elasticum

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Evaluation of Safety, Tolerability, and Efficacy of INZ-701 in Adults With ABCC6 Deficiency Causing PXE
INZ-701 - ATP-Binding Cassette Subfamily C Member 6 Deficiency, Pseudoxanthoma Elasticum
Phase 1 / Phase 2CompletedInozyme Pharma102022-04-112026-10-13
Treatment of Exudative and Vasogenic Chorioretinal Diseases Including Variants of AMD and Other CNV Related Maculopathy
ranibizumab injection (0.5 mg) - Coats' Disease, Idiopathic Retinal Telangiectasia
Phase 1 / Phase 2CompletedManhattan Eye, Ear & Throat Hospital182007-05-012012-10-25

Narrower conditions

Arterial calcification of infancy (1)  ·  Myopia, Degenerative (1)  ·  Polypoidal Choroidal Vasculopathy (1)  ·  Retinal Telangiectasis (1)  ·  Vitelliform Macular Dystrophy (1)  ·  von Hippel-Lindau Disease (1)

Broader conditions

Cardiovascular Diseases (2)  ·  Congenital Abnormalities (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Connective Tissue Diseases (2)  ·  Genetic Diseases, Inborn (2)  ·  Hematologic Diseases (2)  ·  Hemic and Lymphatic Diseases (2)  ·  Hemorrhagic Disorders (2)  ·  Hemostatic Disorders (2)  ·  Skin Abnormalities (2)  ·  Skin Diseases (2)  ·  Skin Diseases, Genetic (2)  ·  Skin and Connective Tissue Diseases (2)  ·  Vascular Diseases (2)  ·  Abnormalities, Multiple (1)

Interventions

Ranibizumab (1)

Sponsors

Inozyme Pharma (1)  ·  Manhattan Eye, Ear & Throat Hospital (1)

Countries

United States (2)  ·  United Kingdom (1)

Top investigators

Lawrence A. Yannuzzi, MD (1)