2 completed, 1 terminated. 3 Phase 1, 2 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 3 | Completed 2, Terminated 1 |
| Phase 2 | 2 | Completed 2 |
Follow Pseudoxanthoma Elasticum: new trials by email Literature Review of Pseudoxanthoma Elasticum trials Research Report on Pseudoxanthoma Elasticum
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| The ENERGY Study: Evaluation of Safety and Tolerability of INZ-701 in Infants With ENPP1 Deficiency or ABCC6 Deficiency INZ-701 - Ectonucleotide Pyrophosphatase/phosphodiesterase1 Deficiency, Autosomal Recessive Hypophosphatemic Rickets | Phase 1 | Terminated | Inozyme Pharma | 9 | 2023-06-25 | 2026-10-15 |
| Evaluation of Safety, Tolerability, and Efficacy of INZ-701 in Adults With ABCC6 Deficiency Causing PXE INZ-701 - ATP-Binding Cassette Subfamily C Member 6 Deficiency, Pseudoxanthoma Elasticum | Phase 1 / Phase 2 | Completed | Inozyme Pharma | 10 | 2022-04-11 | 2026-10-13 |
| Treatment of Exudative and Vasogenic Chorioretinal Diseases Including Variants of AMD and Other CNV Related Maculopathy ranibizumab injection (0.5 mg) - Coats' Disease, Idiopathic Retinal Telangiectasia | Phase 1 / Phase 2 | Completed | Manhattan Eye, Ear & Throat Hospital | 18 | 2007-05-01 | 2012-10-25 |
Arterial calcification of infancy (2) · Hypophosphatemic Rickets, Autosomal Recessive, 1 (1) · Myopia, Degenerative (1) · Polypoidal Choroidal Vasculopathy (1) · Retinal Telangiectasis (1) · Vitelliform Macular Dystrophy (1) · von Hippel-Lindau Disease (1)
Cardiovascular Diseases (3) · Congenital Abnormalities (3) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3) · Connective Tissue Diseases (3) · Genetic Diseases, Inborn (3) · Hematologic Diseases (3) · Hemic and Lymphatic Diseases (3) · Hemorrhagic Disorders (3) · Hemostatic Disorders (3) · Skin Abnormalities (3) · Skin Diseases (3) · Skin Diseases, Genetic (3) · Skin and Connective Tissue Diseases (3) · Vascular Diseases (3) · Abnormalities, Multiple (1)
Ranibizumab (1)
Inozyme Pharma (2) · Manhattan Eye, Ear & Throat Hospital (1)
United States (3) · United Kingdom (2) · Spain (1)