Propionic Acidemia: Clinical Trials

1 trial for Propionic Acidemia, newest first

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1 completed. 1 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 11Completed 1

Follow Propionic Acidemia: new trials by email Literature Review of Propionic Acidemia trials Research Report on Propionic Acidemia

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Anaplerotic Therapy in Propionic Acidemia
ornithine alpha ketoglutarate, glutamine, disodium citrate - Propionic Acidemia
Phase 1CompletedNicola Longo32008-07-012015-01-21

Narrower conditions

Hyperammonemia (1)  ·  Muscle Hypotonia (1)

Broader conditions

Amino Acid Metabolism, Inborn Errors (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Nervous System Diseases (1)  ·  Neurologic Manifestations (1)  ·  Neuromuscular Manifestations (1)  ·  Nutritional and Metabolic Diseases (1)  ·  Pathologic Processes (1)  ·  Pathological Conditions, Signs and Symptoms (1)  ·  Signs and Symptoms (1)

Interventions

Glutamic Acid (1)  ·  Glutamine (1)  ·  Sodium Citrate (1)  ·  ornithine alpha-ketoglutarate (1)

Sponsors

Nicola Longo (1)

Countries

United States (1)

Top investigators

Nicola Longo, MD, PhD (1)

Results publications

PMID 28712602

NIH funding

R21DK077415 (1)