1 completed. 1 Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Completed 1 |
Follow Propionic Acidemia: new trials by email Literature Review of Propionic Acidemia trials Research Report on Propionic Acidemia
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Anaplerotic Therapy in Propionic Acidemia ornithine alpha ketoglutarate, glutamine, disodium citrate - Propionic Acidemia | Phase 1 | Completed | Nicola Longo | 3 | 2008-07-01 | 2015-01-21 |
Hyperammonemia (1) · Muscle Hypotonia (1)
Amino Acid Metabolism, Inborn Errors (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1) · Nervous System Diseases (1) · Neurologic Manifestations (1) · Neuromuscular Manifestations (1) · Nutritional and Metabolic Diseases (1) · Pathologic Processes (1) · Pathological Conditions, Signs and Symptoms (1) · Signs and Symptoms (1)
Glutamic Acid (1) · Glutamine (1) · Sodium Citrate (1) · ornithine alpha-ketoglutarate (1)
Nicola Longo (1)
United States (1)
R21DK077415 (1)