Pediatrics: Clinical Trials

1 trial for Pediatrics, newest first

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1 terminated. 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 21Terminated 1

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TrialPhaseStatusSponsorEnrollmentStartUpdated
Related Hematopoietic Stem Cell Transplantation (HSCT) for Genetic Diseases of Blood Cells
Cyclophosphamide Dose Level 1, Cyclophosphamide Dose Level 2, Cyclophosphamide Dose Level 3 - Stem Cell Transplantation, Bone Marrow Transplantation
Phase 2TerminatedChildren's Hospital Los Angeles202007-02-012017-02-27

Narrower conditions

Anemia, Diamond-Blackfan (1)  ·  Genetic Diseases, Inborn (1)  ·  Granulomatous Disease, Chronic (1)  ·  Lymphoproliferative Disorders (1)  ·  Metabolic Diseases (1)  ·  Thalassemia (1)  ·  Wiskott-Aldrich Syndrome (1)

Broader conditions

Anemia (1)  ·  Anemia, Aplastic (1)  ·  Anemia, Hemolytic (1)  ·  Anemia, Hemolytic, Congenital (1)  ·  Anemia, Hypoplastic, Congenital (1)  ·  Blood Coagulation Disorders (1)  ·  Blood Coagulation Disorders, Inherited (1)  ·  Bone Marrow Diseases (1)  ·  Bone Marrow Failure Disorders (1)  ·  Chronic Disease (1)  ·  Congenital Bone Marrow Failure Syndromes (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Cytopenia (1)  ·  Disease Attributes (1)  ·  Genetic Diseases, X-Linked (1)

Interventions

Cyclophosphamide (1)

Sponsors

Children's Hospital Los Angeles (1)

Top investigators

Neena Kapoor, M.D. (1)

Results publications

PMID 25459642