2 recruiting. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Recruiting 1 |
| Phase 2 | 1 | Recruiting 1 |
Follow NAGS Deficiency: new trials by email Literature Review of NAGS Deficiency trials Research Report on NAGS Deficiency
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Phase 1/2 Study of KRRO-121 in Healthy Volunteers and Patients With UCD KRRO-121, Placebo - Urea Cycle Disorders, Inborn, Urea Cycle Disorders | Phase 1 / Phase 2 | Recruiting | Korro Bio, Inc. | 30 | 2026-09-28 | 2026-10-08 |
| Hepatic Histopathology in Urea Cycle Disorders Urea Cycle Disorder, Ornithine Transcarbamylase Deficiency | Recruiting | Baylor College of Medicine | 70 | 2022-02-24 | 2025-07-20 |
Argininosuccinic Aciduria (2) · Hyperargininemia (2) · N-acetyl glutamate synthetase deficiency (2) · Ornithine Carbamoyltransferase Deficiency Disease (2) · Urea Cycle Disorders, Inborn (2) · Adult-onset citrullinemia type 2 (1) · Carbamoyl-Phosphate Synthase I Deficiency Disease (1) · Citrullinemia (1) · Liver Diseases (1)
Amino Acid Metabolism, Inborn Errors (2) · Brain Diseases (2) · Brain Diseases, Metabolic (2) · Brain Diseases, Metabolic, Inborn (2) · Central Nervous System Diseases (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Genetic Diseases, Inborn (2) · Genetic Diseases, X-Linked (2) · Metabolic Diseases (2) · Metabolism, Inborn Errors (2) · Nervous System Diseases (2) · Nutritional and Metabolic Diseases (2) · Digestive System Diseases (1) · Mitochondrial Diseases (1)
Baylor College of Medicine (1) · Korro Bio, Inc. (1)
Australia (1) · United States (1)