2 active not recruiting, 1 recruiting. 1 Not applicable, 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Not applicable | 1 | Active not recruiting 1 |
| Phase 1 | 1 | Recruiting 1 |
| Phase 2 | 1 | Recruiting 1 |
Follow Adult-onset citrullinemia type 2: new trials by email Literature Review of Adult-onset citrullinemia type 2 trials Research Report on Adult-onset citrullinemia type 2
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Phase 1/2 Study of KRRO-121 in Healthy Volunteers and Patients With UCD KRRO-121, Placebo - Urea Cycle Disorders, Inborn, Urea Cycle Disorders | Phase 1 / Phase 2 | Recruiting | Korro Bio, Inc. | 30 | 2026-09-28 | 2026-10-08 |
| Liver Metabolic Functions in Patients With Citrin Deficiency and Healthy Subjects liver metabolic flux, ureagenesis capacity - Citrin Deficiency | Not applicable | Active not recruiting | Johannes Haeberle | 20 | 2025-10-20 | 2026-01-08 |
| Multi-omics Study in Citrin Deficiency Citrin Deficiency | Active not recruiting | Johannes Haeberle | 100 | 2023-04-01 | 2026-06-02 |
Argininosuccinic Aciduria (1) · Hyperargininemia (1) · N-acetyl glutamate synthetase deficiency (1) · Ornithine Carbamoyltransferase Deficiency Disease (1) · Urea Cycle Disorders, Inborn (1)
Amino Acid Metabolism, Inborn Errors (1) · Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Central Nervous System Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Genetic Diseases, X-Linked (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1) · Nervous System Diseases (1) · Nutritional and Metabolic Diseases (1)
Johannes Haeberle (2) · Korro Bio, Inc. (1)
Australia (1) · Japan (1) · South Korea (1) · Switzerland (1) · Taiwan (1) · United Kingdom (1) · United States (1)
2025 (1)