Myotonic Dystrophy Type 2: Clinical Trials

5 trials for Myotonic Dystrophy Type 2, newest first

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2 completed, 1 enrolling by invitation, 1 recruiting, 1 unknown. .

Follow Myotonic Dystrophy Type 2: new trials by email Literature Review of Myotonic Dystrophy Type 2 trials Research Report on Myotonic Dystrophy Type 2

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Brain Structure and Clinical Endpoints in Myotonic Dystrophy Type 2
Non-interventional study - Myotonic Dystrophy Type 2, Myotonic Dystrophy Type 1
Enrolling by invitationWake Forest University Health Sciences1002023-04-262026-07-14
Musculoskeletal Nociceptive Pain in Participants With Neuromuscular Disorders
Beck depression inventory fast screen, German Pain Inventory, Brief Pain Inventory - Pompe Disease (Late-onset), Myotonic Dystrophy Type 1 (DM1)
CompletedLMU Klinikum822021-04-152022-08-24
Clinical Outcome Measures in Myotonic Dystrophy Type 2
DM1-ActivC, R-PAct, Beck depression inventory - Myotonic Dystrophy Type 2
CompletedProf. Dr. Benedikt Schoser602018-07-012020-02-20
Muscle Relaxation in Myopathies With Positive Muscle Phenomena
Transcranial magnetic stimulation (TMS) - Nemaline Myopathy Type 6, Myotonic Dystrophy Type 2
UnknownRadboud University Medical Center302017-01-052019-10-01
Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry
Myotonic Dystrophy, Facioscapulohumeral Muscular Dystrophy
RecruitingUniversity of Rochester30002000-09-012025-10-15

Narrower conditions

Myotonic Dystrophy (5)  ·  Muscular Dystrophies (2)  ·  Cognitive Dysfunction (1)  ·  Glycogen Storage Disease Type II (1)  ·  Glycogen Storage Disease Type V (1)  ·  Muscular Diseases (1)  ·  Muscular Dystrophy, Facioscapulohumeral (1)  ·  Myositis, Inclusion Body (1)  ·  Neurodegenerative Diseases (1)  ·  Nociceptive Pain (1)  ·  Spinal Muscular Atrophies of Childhood (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (5)  ·  Genetic Diseases, Inborn (5)  ·  Heredodegenerative Disorders, Nervous System (5)  ·  Muscular Disorders, Atrophic (5)  ·  Musculoskeletal Diseases (5)  ·  Myotonic Disorders (5)  ·  Nervous System Diseases (5)  ·  Neuromuscular Diseases (5)  ·  Muscular Diseases (4)  ·  Neurodegenerative Diseases (4)  ·  Muscular Dystrophies (3)  ·  Carbohydrate Metabolism, Inborn Errors (2)  ·  Glycogen Storage Disease (2)  ·  Metabolic Diseases (2)  ·  Metabolism, Inborn Errors (2)

Interventions

Pain Measurement (1)  ·  Physical Examination (1)  ·  Vital Signs (1)  ·  Walk Test (1)

Sponsors

LMU Klinikum (1)  ·  Prof. Dr. Benedikt Schoser (1)  ·  Radboud University Medical Center (1)  ·  University of Rochester (1)  ·  Wake Forest University Health Sciences (1)

Countries

Germany (2)  ·  United States (2)

Top investigators

Araya Puwanant, MD, MS (1)  ·  Baziel G van Engelen, MD, PhD (1)  ·  Benedikt Schoser, MD (1)  ·  Johann Hamel, MD (1)  ·  Stephan Wenninger, PD Dr. med. (1)

Results publications

PMID 32373059

NIH funding

K23NS125110 (1), U54NS048843 (1)