1 completed, 1 terminated, 1 withdrawn. 3 Phase 1, 2 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 3 | Completed 1, Terminated 1, Withdrawn 1 |
| Phase 2 | 2 | Completed 1, Withdrawn 1 |
Follow Myopathy: new trials by email Literature Review of Myopathy trials Research Report on Myopathy
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Therapeutic Effect of Recombinant Human Growth Hormone (rhGH) on the Myopathy of Cystinosis rh Growth Hormone - Cystinosis, Myopathy | Phase 1 / Phase 2 | Withdrawn | National Human Genome Research Institute (NHGRI) | 2014-03-26 | 2017-10-20 | |
| EPI-743 for Metabolism or Mitochondrial Disorders EPI-743, Placebo - Mitochondrial Disease, Neurology | Phase 1 / Phase 2 | Completed | National Human Genome Research Institute (NHGRI) | 20 | 2012-09-01 | 2021-04-14 |
| Stem Cell Transplantation in Idiopathic Inflammatory Myopathy Diseases Hematopoietic stem cell transplantation, Cyclophosphamide, Mesna - MYOPATHY | Phase 1 | Terminated | Northwestern University | 7 | 2005-09-01 | 2018-08-06 |
Muscular Diseases (3) · Cystinosis (1) · Mitochondrial Diseases (1)
Musculoskeletal Diseases (3) · Nervous System Diseases (3) · Neuromuscular Diseases (3) · Metabolic Diseases (2) · Nutritional and Metabolic Diseases (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Lysosomal Storage Diseases (1) · Metabolism, Inborn Errors (1)
Cyclophosphamide (1) · Granulocyte Colony-Stimulating Factor (1) · Hematopoietic Stem Cell Transplantation (1) · Mesna (1) · Methylprednisolone (1) · Rituximab (1) · alpha-tocotrienol quinone (1) · thymoglobulin (1)
National Human Genome Research Institute (NHGRI) (2) · Northwestern University (1)
United States (2)
Galina V Nesterova, M.D. (1) · Richard Burt, MD (1) · William A Gahl, M.D. (1)