1 recruiting. .
Follow MPS III: new trials by email Literature Review of MPS III trials Research Report on MPS III
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Longitudinal Study of Neurodegenerative Disorders Palliative Care, Hematopoetic Stem Cell Transplantation - MLD, Krabbe Disease | Recruiting | University of Pittsburgh | 1500 | 2012-01-11 | 2026-02-09 |
Gaucher Disease (1) · Hypermethioninemia (1) · Language (1) · Leukodystrophy, Globoid Cell (1) · Leukoencephalopathies (1) · Lysosomal Storage Diseases (1) · Mucopolysaccharidosis III (1) · Mucopolysaccharidosis IV (1) · Multiple Sulfatase Deficiency Disease (1) · Neuronal Ceroid-Lipofuscinoses (1) · Niemann-Pick Diseases (1) · Osteopetrosis (1) · Pelizaeus-Merzbacher Disease (1) · Purine Nucleoside Phosphorylase Deficiency (1) · Sandhoff Disease (1)
Behavior (1) · Bone Diseases (1) · Bone Diseases, Developmental (1) · Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Carbohydrate Metabolism, Inborn Errors (1) · Central Nervous System Diseases (1) · Communication (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Connective Tissue Diseases (1) · Death (1) · Death, Sudden (1) · Demyelinating Diseases (1) · Gangliosidoses (1)
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United States (1)