Leber Hereditary Optic Neuropathy: Clinical Trials

1 trial for Leber Hereditary Optic Neuropathy, newest first

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1 completed. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Completed 1
Phase 21Completed 1

Follow Leber Hereditary Optic Neuropathy: new trials by email Literature Review of Leber Hereditary Optic Neuropathy trials Research Report on Leber Hereditary Optic Neuropathy

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Safety Evaluation of Gene Therapy in Leber Hereditary Optic Neuropathy (LHON) Patients
GS010 - Leber Hereditary Optic Neuropathy
Phase 1 / Phase 2CompletedGenSight Biologics192014-02-132026-03-02

Narrower conditions

Optic Atrophy, Hereditary, Leber (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Cranial Nerve Diseases (1)  ·  Eye Diseases (1)  ·  Eye Diseases, Hereditary (1)  ·  Genetic Diseases, Inborn (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Metabolic Diseases (1)  ·  Mitochondrial Diseases (1)  ·  Nervous System Diseases (1)  ·  Neurodegenerative Diseases (1)  ·  Nutritional and Metabolic Diseases (1)  ·  Optic Atrophies, Hereditary (1)  ·  Optic Atrophy (1)  ·  Optic Nerve Diseases (1)

Sponsors

GenSight Biologics (1)

Countries

France (1)