Homocystinuria: Clinical Trials

3 trials for Homocystinuria, newest first

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3 completed. 3 Phase 2, 1 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 23Completed 3
Phase 11Completed 1

Follow Homocystinuria: new trials by email Literature Review of Homocystinuria trials Research Report on Homocystinuria

Trials (filtered) newest first · largest first

All 3 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Betaine METABOLISM OF PATIENTS With Homocystinuria
Betaine - Homocystinuria
Phase 2CompletedAssistance Publique - Hôpitaux de Paris122015-07-012023-02-03
Oxidative Stress Markers In Inherited Homocystinuria And The Impact Of Taurine
taurine - Homocystinuria
Phase 1 / Phase 2CompletedUniversity of Colorado, Denver152010-01-012018-07-09
Homocystinuria: Treatment With N-Acetylcysteine
N-acetylcysteine - Homocystinuria
Phase 2CompletedMcGill University Health Centre/Research Institute of the McGill University Health Centre52007-11-012009-02-18

Broader conditions

Amino Acid Metabolism, Inborn Errors (3)  ·  Brain Diseases (3)  ·  Brain Diseases, Metabolic (3)  ·  Brain Diseases, Metabolic, Inborn (3)  ·  Central Nervous System Diseases (3)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3)  ·  Connective Tissue Diseases (3)  ·  Genetic Diseases, Inborn (3)  ·  Hyperhomocysteinemia (3)  ·  Metabolic Diseases (3)  ·  Metabolism, Inborn Errors (3)  ·  Nervous System Diseases (3)  ·  Nutritional and Metabolic Diseases (3)  ·  Skin and Connective Tissue Diseases (3)

Interventions

Acetylcysteine (1)  ·  Betaine (1)  ·  Taurine (1)

Sponsors

Assistance Publique - Hôpitaux de Paris (1)  ·  McGill University Health Centre/Research Institute of the McGill University Health Centre (1)  ·  University of Colorado, Denver (1)

Countries

Canada (1)  ·  France (1)  ·  United States (1)

Top investigators

Johan VanHove, MD PhD MBA (1)

Results publications

PMID 36376887