Hemoglobinuria: Clinical Trials

2 trials for Hemoglobinuria, newest first

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2 completed. 2 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 12Completed 2

Follow Hemoglobinuria: new trials by email Literature Review of Hemoglobinuria trials Research Report on Hemoglobinuria

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Pilot Study to Assess Safety, Preliminary Efficacy and Pharmacokinetics of S.C. Pegcetacoplan (APL-2) in PNH Subjects.
Pegcetacoplan - Paroxysmal Nocturnal Hemoglobinuria
Phase 1CompletedApellis Pharmaceuticals, Inc.232015-12-012021-01-11
A Phase I Study to Assess the Safety of Pegcetacoplan (APL-2) as an Add-On to Standard of Care in Subjects With PNH
Pegcetacoplan - Paroxysmal Nocturnal Hemoglobinuria (PNH)
Phase 1CompletedApellis Pharmaceuticals, Inc.92015-02-232021-01-08

Narrower conditions

Anemia (2)  ·  Hematologic Diseases (2)  ·  Hemoglobinuria, Paroxysmal (2)  ·  Hemolysis (2)

Broader conditions

Anemia, Hemolytic (2)  ·  Bone Marrow Diseases (2)  ·  Female Urogenital Diseases (2)  ·  Female Urogenital Diseases and Pregnancy Complications (2)  ·  Hemic and Lymphatic Diseases (2)  ·  Male Urogenital Diseases (2)  ·  Myelodysplastic Syndromes (2)  ·  Pathologic Processes (2)  ·  Pathological Conditions, Signs and Symptoms (2)  ·  Proteinuria (2)  ·  Signs and Symptoms (2)  ·  Urination Disorders (2)  ·  Urogenital Diseases (2)  ·  Urologic Diseases (2)  ·  Urological Manifestations (2)

Interventions

pegcetacoplan (2)

Sponsors

Apellis Pharmaceuticals, Inc. (2)

Countries

Hong Kong (1)  ·  Malaysia (1)  ·  New Zealand (1)  ·  Thailand (1)  ·  United States (1)

Top investigators

Federico Grossi, MD, PhD (2)

Results publications

PMID 35869170, PMID 39079163