1 completed. .
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Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Longitudinal Studies of the Glycoproteinoses Non-interventional. - Aspartylglucosaminuria, Fucosidosis | Completed | Greenwood Genetic Center | 100 | 2009-08-01 | 2023-09-13 |
Aspartylglucosaminuria (1) · Fucosidosis (1) · Lysosomal Storage Diseases (1) · Metabolic Diseases (1) · Mucolipidoses (1) · Neuraminidase deficiency with beta-galactosidase deficiency (1) · Schindler Disease, Type I (1) · alpha-Mannosidosis (1) · beta-Mannosidosis (1)
Bone Diseases (1) · Bone Diseases, Metabolic (1) · Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Carbohydrate Metabolism, Inborn Errors (1) · Central Nervous System Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Lysosomal Storage Diseases, Nervous System (1) · Mannosidase Deficiency Diseases (1) · Metabolism, Inborn Errors (1) · Musculoskeletal Diseases (1) · Nervous System Diseases (1) · Nutritional and Metabolic Diseases (1)
United States (1)
Sara Cathey, MD (1)