Genetic Disorder: Clinical Trials

2 trials for Genetic Disorder, newest first

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2 terminated. 2 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 22Terminated 2

Follow Genetic Disorder: new trials by email Literature Review of Genetic Disorder trials Research Report on Genetic Disorder

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Pharmacokinetics of Thymoglobulin in Paediatric Haematopoietic Stem-cell Transplants
Thymoglobulin (rATG) - Malignancy, Metabolic Disease
Phase 2TerminatedThe Hospital for Sick Children302009-11-012019-11-04
Fludarabine Phosphate, Cyclophosphamide, and Total-Body Irradiation Followed by Donor Bone Marrow Transplant and Cyclophosphamide, Mycophenolate Mofetil, Tacrolimus, and Sirolimus in Treating Patients With Primary Immunodeficiency Disorders or Noncancerous Inherited Disorders
Allogeneic Bone Marrow Transplantation, Cyclophosphamide, Fludarabine Phosphate - Immunodeficiency Syndrome, Severe Aplastic Anemia
Phase 2TerminatedFred Hutchinson Cancer Center142006-05-242021-01-26

Narrower conditions

Genetic Diseases, Inborn (2)  ·  Anemia, Aplastic (1)  ·  Immunologic Deficiency Syndromes (1)  ·  Metabolic Diseases (1)  ·  Neoplasms (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Anemia (1)  ·  Bone Marrow Diseases (1)  ·  Bone Marrow Failure Disorders (1)  ·  Hematologic Diseases (1)  ·  Hemic and Lymphatic Diseases (1)  ·  Immune System Diseases (1)  ·  Nutritional and Metabolic Diseases (1)

Interventions

Antilymphocyte Serum (1)  ·  Cyclophosphamide (1)  ·  Mycophenolic Acid (1)  ·  Sirolimus (1)  ·  Tacrolimus (1)  ·  Whole-Body Irradiation (1)  ·  fludarabine phosphate (1)  ·  thymoglobulin (1)

Sponsors

Fred Hutchinson Cancer Center (1)  ·  The Hospital for Sick Children (1)

Countries

Canada (1)  ·  United States (1)

Top investigators

Kanwaldeep Mallhi (1)  ·  Tal Schechter-Finkelstein, MD (1)

NIH funding

P01HL122173 (1), P30CA015704 (1)