1 completed. 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 3 | 1 | Completed 1 |
Follow Gene Therapy: new trials by email Literature Review of Gene Therapy trials Research Report on Gene Therapy
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Gene Replacement Therapy Clinical Trial for Participants With Spinal Muscular Atrophy Type 1 Onasemnogene Abeparvovec-xioi - SMA - Spinal Muscular Atrophy, Gene Therapy | Phase 3 | Completed | Novartis Gene Therapies | 22 | 2017-10-24 | 2026-01-26 |
Central Nervous System Diseases (1) · Motor Neuron Disease (1) · Nervous System Diseases (1) · Neurodegenerative Diseases (1) · Neuromuscular Diseases (1) · Spinal Cord Diseases (1)
Zolgensma (1)
United States (1)