Friedreich Ataxia: Clinical Trials

1 trial for Friedreich Ataxia, newest first

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1 terminated. 1 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 11Terminated 1

Follow Friedreich Ataxia: new trials by email Literature Review of Friedreich Ataxia trials Research Report on Friedreich Ataxia

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Study to Assess Nomlabofusp in Adolescents and Children With Friedreich's Ataxia
Nomlabofusp, Placebo - Friedreich Ataxia
Phase 1TerminatedLarimar Therapeutics, Inc.182024-12-062026-07-10

Broader conditions

Brain Diseases (1)  ·  Central Nervous System Diseases (1)  ·  Cerebellar Diseases (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Metabolic Diseases (1)  ·  Mitochondrial Diseases (1)  ·  Nervous System Diseases (1)  ·  Neurodegenerative Diseases (1)  ·  Nutritional and Metabolic Diseases (1)  ·  Spinal Cord Diseases (1)  ·  Spinocerebellar Degenerations (1)

Sponsors

Larimar Therapeutics, Inc. (1)

Countries

United States (1)