1 terminated. 1 Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Terminated 1 |
Follow Friedreich Ataxia: new trials by email Literature Review of Friedreich Ataxia trials Research Report on Friedreich Ataxia
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Study to Assess Nomlabofusp in Adolescents and Children With Friedreich's Ataxia Nomlabofusp, Placebo - Friedreich Ataxia | Phase 1 | Terminated | Larimar Therapeutics, Inc. | 18 | 2024-12-06 | 2026-07-10 |
Brain Diseases (1) · Central Nervous System Diseases (1) · Cerebellar Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Heredodegenerative Disorders, Nervous System (1) · Metabolic Diseases (1) · Mitochondrial Diseases (1) · Nervous System Diseases (1) · Neurodegenerative Diseases (1) · Nutritional and Metabolic Diseases (1) · Spinal Cord Diseases (1) · Spinocerebellar Degenerations (1)
Larimar Therapeutics, Inc. (1)
United States (1)