Cirrhosis, Cryptogenic: Clinical Trials

1 trial for Cirrhosis, Cryptogenic, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

1 terminated. 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 21Terminated 1

Follow Cirrhosis, Cryptogenic: new trials by email Literature Review of Cirrhosis, Cryptogenic trials Research Report on Cirrhosis, Cryptogenic

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Clinical Study In Infants With Rapidly Progressive Lysosomal Acid Lipase Deficiency
Sebelipase Alfa - Lysosomal Acid Lipase Deficiency
Phase 2TerminatedAlexion Pharmaceuticals, Inc.102014-06-062019-11-18

Narrower conditions

Chanarin-Dorfman Syndrome (1)  ·  Cholesterol Ester Storage Disease (1)  ·  Liver Diseases, Alcoholic (1)  ·  Niemann-Pick Diseases (1)  ·  Non-alcoholic Fatty Liver Disease (1)  ·  Wolman Disease (1)

Broader conditions

Alcohol-Induced Disorders (1)  ·  Alcohol-Related Disorders (1)  ·  Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Central Nervous System Diseases (1)  ·  Chemically-Induced Disorders (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Digestive System Diseases (1)  ·  Fatty Liver (1)  ·  Genetic Diseases, Inborn (1)  ·  Hemic and Lymphatic Diseases (1)  ·  Histiocytosis (1)  ·  Histiocytosis, Non-Langerhans-Cell (1)  ·  Infant, Newborn, Diseases (1)

Interventions

Sebelipase alfa (1)

Sponsors

Alexion Pharmaceuticals, Inc. (1)

Countries

Finland (1)  ·  Italy (1)  ·  United Kingdom (1)  ·  United States (1)