1 completed, 1 terminated. 2 Phase 2, 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 2 | Completed 1, Terminated 1 |
| Phase 3 | 1 | Completed 1 |
Follow Cirrhosis, Cryptogenic: new trials by email Literature Review of Cirrhosis, Cryptogenic trials Research Report on Cirrhosis, Cryptogenic
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Clinical Study In Infants With Rapidly Progressive Lysosomal Acid Lipase Deficiency Sebelipase Alfa - Lysosomal Acid Lipase Deficiency | Phase 2 | Terminated | Alexion Pharmaceuticals, Inc. | 10 | 2014-06-06 | 2019-11-18 |
| Safety, Tolerability, Efficacy, Pharmacokinetics, and Pharmacodynamics of Sebelipase Alfa in Children With Growth Failure Due to Lysosomal Acid Lipase Deficiency Sebelipase alfa (SBC-102) - Lysosomal Acid Lipase Deficiency, Wolman Disease | Phase 2 / Phase 3 | Completed | Alexion Pharmaceuticals, Inc. | 9 | 2011-05-04 | 2019-01-30 |
Chanarin-Dorfman Syndrome (2) · Cholesterol Ester Storage Disease (2) · Liver Diseases, Alcoholic (2) · Niemann-Pick Diseases (2) · Non-alcoholic Fatty Liver Disease (2) · Wolman Disease (2)
Alcohol-Induced Disorders (2) · Alcohol-Related Disorders (2) · Brain Diseases (2) · Brain Diseases, Metabolic (2) · Brain Diseases, Metabolic, Inborn (2) · Central Nervous System Diseases (2) · Chemically-Induced Disorders (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Digestive System Diseases (2) · Fatty Liver (2) · Genetic Diseases, Inborn (2) · Hemic and Lymphatic Diseases (2) · Histiocytosis (2) · Histiocytosis, Non-Langerhans-Cell (2) · Infant, Newborn, Diseases (2)
Sebelipase alfa (2)
Alexion Pharmaceuticals, Inc. (2)
United Kingdom (2) · United States (2) · Egypt (1) · Finland (1) · France (1) · Ireland (1) · Italy (1)