1 completed. 1 Phase 2, 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 1 | Completed 1 |
| Phase 3 | 1 | Completed 1 |
Follow Batten Disease: new trials by email Literature Review of Batten Disease trials Research Report on Batten Disease
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Stem Cell Transplant for Inborn Errors of Metabolism Stem Cell Transplant, Busulfan, Cyclophosphamide, Antithymocyte Globulin - Adrenoleukodystrophy, Metachromatic Leukodystrophy | Phase 2 / Phase 3 | Completed | Masonic Cancer Center, University of Minnesota | 135 | 1995-01-01 | 2017-12-28 |
Adrenoleukodystrophy (1) · Fucosidosis (1) · Gangliosidosis, GM1 (1) · Gaucher Disease (1) · Leukodystrophy, Globoid Cell (1) · Leukodystrophy, Metachromatic (1) · Neuronal Ceroid-Lipofuscinoses (1) · Niemann-Pick Diseases (1) · Sandhoff Disease (1) · Tay-Sachs Disease (1) · Wolman Disease (1)
Adrenal Gland Diseases (1) · Adrenal Insufficiency (1) · Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Carbohydrate Metabolism, Inborn Errors (1) · Central Nervous System Diseases (1) · Cholesterol Ester Storage Disease (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Demyelinating Diseases (1) · Endocrine System Diseases (1) · Gangliosidoses (1) · Gangliosidoses, GM2 (1) · Genetic Diseases, Inborn (1) · Genetic Diseases, X-Linked (1)
Antilymphocyte Serum (1) · Bone Marrow Transplantation (1) · Busulfan (1) · Cyclophosphamide (1) · Stem Cell Transplantation (1)
Masonic Cancer Center, University of Minnesota (1)
United States (1)
Paul Orchard, MD (1)