ATTR Amyloidosis: Clinical Trials

7 trials for ATTR Amyloidosis, newest first

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4 recruiting, 2 completed, 1 unknown. 1 Phase 2, 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 21Completed 1
Phase 31Completed 1

Follow ATTR Amyloidosis: new trials by email Literature Review of ATTR Amyloidosis trials Research Report on ATTR Amyloidosis

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Hungarian National Systemic Amyloidosis Registry
Systemic Amyloidosis, ATTR Amyloidosis
RecruitingSemmelweis University3002026-03-082026-07-08
Orthopaedic Specimen Pathology and Early Diagnosis of ATTR Cardiopathy (ATTR-ORTHO)
ATTR Amyloidosis, Cardiopathy
UnknownInstitut Mutualiste Montsouris1502024-02-272024-04-16
OverTTuRe: Characteristics, Treatment Patterns and Outcomes of Patients With ATTR Amyloidosis
no intervention - ATTR Amyloidosis
RecruitingAstraZeneca521212023-08-212026-09-09
Efficacy of [18F]Florbetaben PET for Diagnosis of Cardiac AL Amyloidosis
[18F]florbetaben - Cardiac Amyloidosis, AL Amyloidosis
Phase 3CompletedLantheus Germany GmbH2442023-01-132026-08-03
The Italian Transthyretin Amyloidosis Web-Network
ATTR Amyloidosis
RecruitingFondazione IRCCS Policlinico San Matteo di Pavia10002022-07-132026-03-27
ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis)
Transthyretin-Mediated Amyloidosis, ATTR Amyloidosis
RecruitingAlnylam Pharmaceuticals15002020-11-232026-10-13
The Study of an Investigational Drug, Revusiran (ALN-TTRSC), for the Treatment of Transthyretin (TTR)-Mediated Amyloidosis in Patients Whose Disease Has Continued to Worsen Following Liver Transplant
Revusiran - Transthyretin (TTR)-Mediated Amyloidosis, Familial Amyloidotic Polyneuropathy (FAP)
Phase 2CompletedAlnylam Pharmaceuticals122015-10-012019-03-28

Narrower conditions

Amyloid Neuropathies, Familial (5)  ·  Immunoglobulin Light-chain Amyloidosis (3)  ·  Amyloidosis (2)  ·  Amyloid Neuropathies (1)  ·  Amyloidosis, Familial (1)  ·  Amyloidosis, Hereditary, Transthyretin-Related (1)  ·  Carpal Tunnel Syndrome (1)  ·  Heart Diseases (1)  ·  Polyneuropathies (1)

Broader conditions

Metabolic Diseases (6)  ·  Nutritional and Metabolic Diseases (6)  ·  Proteostasis Deficiencies (6)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (5)  ·  Genetic Diseases, Inborn (5)  ·  Heredodegenerative Disorders, Nervous System (5)  ·  Metabolism, Inborn Errors (5)  ·  Nervous System Diseases (5)  ·  Neurodegenerative Diseases (5)  ·  Neuromuscular Diseases (5)  ·  Peripheral Nervous System Diseases (5)  ·  Amyloid Neuropathies (4)  ·  Amyloidosis (4)  ·  Amyloidosis, Familial (4)  ·  Immune System Diseases (3)

Interventions

4-(N-methylamino)-4'-(2-(2-(2-fluoroethoxy)ethoxy)ethoxy)stilbene (1)  ·  revusiran (1)

Sponsors

Alnylam Pharmaceuticals (2)  ·  AstraZeneca (1)  ·  Fondazione IRCCS Policlinico San Matteo di Pavia (1)  ·  Institut Mutualiste Montsouris (1)  ·  Lantheus Germany GmbH (1)  ·  Semmelweis University (1)

Countries

Germany (4)  ·  Spain (4)  ·  France (3)  ·  Italy (3)  ·  Portugal (3)  ·  United Kingdom (3)  ·  United States (3)  ·  Denmark (2)  ·  Sweden (2)  ·  Brazil (1)  ·  Bulgaria (1)  ·  Canada (1)  ·  China (1)  ·  Hungary (1)  ·  Israel (1)

Top investigators

Andrew Stephens, MD, PhD (1)  ·  John Vest, MD (1)  ·  Zoltan Pozsonyi, MD, PhD (1)

Results publications

PMID 40108078, PMID 42201638