2 recruiting, 1 completed, 1 withdrawn. 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 1 | Recruiting 1 |
Follow Angiokeratoma: new trials by email Literature Review of Angiokeratoma trials Research Report on Angiokeratoma
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Phase 2, Baseline-Controlled Study Evaluating the Safety and Efficacy of PTX-022 (Sirolimus) Topical Gel 3.9% in the Treatment of Angiokeratomas (LOTU) PTX-022 - Angiokeratomas | Phase 2 | Recruiting | Palvella Therapeutics, Inc. | 15 | 2026-04-01 | 2026-04-27 |
| Understanding Fabry Disease Therapy Choices Through the Eyes of the Patients This is a non-interventional study - Fabry Disease | Completed | Amicus Therapeutics | 44 | 2023-03-01 | 2024-04-03 | |
| Biomarker for Patients With Fabry Disease (BioFabry) Angiokeratomas, Chronic Kidney Disease | Withdrawn | CENTOGENE GmbH Rostock | 2018-08-20 | 2023-02-13 | ||
| Fabry Disease Registry & Pregnancy Sub-registry Fabry Disease | Recruiting | Genzyme, a Sanofi Company | 9000 | 2001-07-31 | 2026-10-14 |
Fabry Disease (3) · Hearing Loss (1) · Hypohidrosis (1) · Proteinuria (1) · Renal Insufficiency, Chronic (1)
Neoplasms (4) · Neoplasms by Histologic Type (4) · Neoplasms, Vascular Tissue (4) · Brain Diseases (3) · Brain Diseases, Metabolic (3) · Brain Diseases, Metabolic, Inborn (3) · Cardiovascular Diseases (3) · Central Nervous System Diseases (3) · Cerebral Small Vessel Diseases (3) · Cerebrovascular Disorders (3) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3) · Genetic Diseases, Inborn (3) · Genetic Diseases, X-Linked (3) · Lipid Metabolism Disorders (3) · Lipid Metabolism, Inborn Errors (3)
Amicus Therapeutics (1) · CENTOGENE GmbH Rostock (1) · Genzyme, a Sanofi Company (1) · Palvella Therapeutics, Inc. (1)
United States (3) · Germany (2) · India (2) · Argentina (1) · Australia (1) · Belgium (1) · Brazil (1) · Bulgaria (1) · Canada (1) · Chile (1) · China (1) · Colombia (1) · Croatia (1) · Czechia (1) · Denmark (1)
Niloofar Nobakht, MD (1) · Peter Bauer, Prof. (1)