Alström Syndrome: Clinical Trials

2 trials for Alström Syndrome, newest first

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1 recruiting, 1 terminated. 1 Not applicable, 1 Phase 2, 1 Phase 3.

By phase and status

PhaseTrialsStatus
Not applicable1Recruiting 1
Phase 21Terminated 1
Phase 31Terminated 1

Follow Alström Syndrome: new trials by email Literature Review of Alström Syndrome trials Research Report on Alström Syndrome

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
COhort for Bardet-Bield Syndrome and Alström Syndrome for Translational Research Monocentric Interventional Study
Skin biopsy - Bardet-Biedl Syndrome, Alström Syndrome
Not applicableRecruitingUniversity Hospital, Strasbourg, France3502020-06-162021-09-10
Open-Label Rollover Study of PBI 4050 in Subjects With Alström Syndrome
PBI-4050 - Alström Syndrome
Phase 2 / Phase 3TerminatedLiminal BioSciences Ltd.102017-10-092020-11-03

Narrower conditions

Alstrom Syndrome (2)  ·  Bardet-Biedl Syndrome (1)

Broader conditions

Abnormalities, Multiple (2)  ·  Ciliopathies (2)  ·  Congenital Abnormalities (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Eye Diseases (2)  ·  Eye Diseases, Hereditary (2)  ·  Genetic Diseases, Inborn (2)  ·  Hereditary Sensory and Motor Neuropathy (2)  ·  Heredodegenerative Disorders, Nervous System (2)  ·  Nervous System Diseases (2)  ·  Nervous System Malformations (2)  ·  Neurodegenerative Diseases (2)  ·  Neuromuscular Diseases (2)  ·  Peripheral Nervous System Diseases (2)  ·  Polyneuropathies (2)

Interventions

setogepram (1)

Sponsors

Liminal BioSciences Ltd. (1)  ·  University Hospital, Strasbourg, France (1)

Countries

France (1)  ·  United Kingdom (1)