1 active not recruiting. 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 1 | Active not recruiting 1 |
Follow Alpha-Methylacyl-CoA Racemase Deficiency: new trials by email Literature Review of Alpha-Methylacyl-CoA Racemase Deficiency trials Research Report on Alpha-Methylacyl-CoA Racemase Deficiency
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis Stem Cell Transplantation, IMD Preparative Regimen, Osteopetrosis Only Preparative Regimen - Mucopolysaccharidosis Disorders, Hurler Syndrome | Phase 2 | Active not recruiting | Masonic Cancer Center, University of Minnesota | 149 | 2014-07-10 | 2026-01-07 |
Aspartylglucosaminuria (1) · Fucosidosis (1) · Hereditary Diffuse Leukoencephalopathy with Spheroids (1) · Leukodystrophy, Globoid Cell (1) · Leukodystrophy, Metachromatic (1) · Mucopolysaccharidosis I (1) · Mucopolysaccharidosis II (1) · Mucopolysaccharidosis VI (1) · Mucopolysaccharidosis VII (1) · Osteopetrosis (1) · Peroxisomal ACYL-COA oxidase deficiency (1) · Peroxisomal Disorders (1) · Pseudo-Zellweger syndrome (1) · Refsum Disease, Infantile (1)
Abnormalities, Multiple (1) · Bone Diseases (1) · Bone Diseases, Developmental (1) · Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Carbohydrate Metabolism, Inborn Errors (1) · Central Nervous System Diseases (1) · Congenital Abnormalities (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Connective Tissue Diseases (1) · Demyelinating Diseases (1) · Digestive System Diseases (1) · Female Urogenital Diseases (1) · Female Urogenital Diseases and Pregnancy Complications (1)
Regimen B (1) · Stem Cell Transplantation (1)
Masonic Cancer Center, University of Minnesota (1)
United States (1)