Albinism: Clinical Trials

5 trials for Albinism, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

2 completed, 1 not yet recruiting, 1 terminated, 1 unknown. 5 Phase 3, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 35Completed 2, Not yet recruiting 1, Terminated 1, Unknown 1
Phase 21Terminated 1

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Trials (filtered) newest first · largest first

All 5 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Preoperative Imatinib Mesylate Combined With Rectal-sparing Surgery in Patients With c-KIT Gene-mutant Rectal GIST
Imatinib Mesylate, Local resection - Gastrointestinal Stromal Tumor of Rectum
Phase 3Not yet recruitingFujian Medical University Union Hospital232023-10-012023-08-01
Masitinib in Severe Indolent or Smoldering Systemic Mastocytosis Unresponsive to Optimal Symptomatic Treatment
Masitinib, Placebo, Best Supportive Care - Indolent Systemic Mastocytosis
Phase 3UnknownAB Science1402020-07-012023-05-06
Evaluation of Non-cultured Epidermal Cellular Grafting vs Hyaluronic Acid for Repigmenting Vitiligo and Piebaldism
VITICELL, PLACEBO - Vitiligo, Piebaldism
Phase 3CompletedLaboratoires Genévrier382014-04-292019-10-14
Masitinib in Severe Indolent or Smoldering Systemic Mastocytosis
Masitinib, Placebo, Best Supportive Care - Indolent Systemic Mastocytosis
Phase 3CompletedAB Science1352008-12-012019-12-03
T-Cell Depletion and Stem Cell Transplant for Immune Deficiencies and Histiocytic Disorders
Stem Cell Transplant, Myeloablative conditioning regimen - Hemophagocytic Lymphohistiocytosis, X-Linked Lymphoproliferative Disorders
Phase 2 / Phase 3TerminatedMasonic Cancer Center, University of Minnesota222000-09-012018-01-23

Narrower conditions

Piebaldism (4)  ·  Blushing (2)  ·  Mastocytosis (2)  ·  Mastocytosis, Systemic (2)  ·  Pruritus (2)  ·  Chediak-Higashi Syndrome (1)  ·  Gastrointestinal Stromal Tumors (1)  ·  Hematologic Diseases (1)  ·  Histiocytosis, Langerhans-Cell (1)  ·  Immune System Diseases (1)  ·  Lymphohistiocytosis, Hemophagocytic (1)  ·  Lymphoproliferative Disorders (1)  ·  Vitiligo (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (5)  ·  Eye Diseases, Hereditary (5)  ·  Genetic Diseases, Inborn (5)  ·  Amino Acid Metabolism, Inborn Errors (4)  ·  Hypopigmentation (4)  ·  Metabolic Diseases (4)  ·  Metabolism, Inborn Errors (4)  ·  Nutritional and Metabolic Diseases (4)  ·  Pigmentation Disorders (4)  ·  Skin Diseases (4)  ·  Skin Diseases, Genetic (4)  ·  Skin and Connective Tissue Diseases (4)  ·  Neoplasms (3)  ·  Neoplasms by Histologic Type (3)

Interventions

masitinib (2)  ·  Busulfan (1)  ·  Cyclophosphamide (1)  ·  Imatinib Mesylate (1)  ·  Mastectomy, Segmental (1)  ·  Stem Cell Transplantation (1)

Sponsors

AB Science (2)  ·  Fujian Medical University Union Hospital (1)  ·  Laboratoires Genévrier (1)  ·  Masonic Cancer Center, University of Minnesota (1)

Countries

France (3)  ·  United States (2)  ·  Belgium (1)  ·  China (1)  ·  Germany (1)  ·  Italy (1)  ·  Netherlands (1)  ·  Poland (1)  ·  Romania (1)  ·  Russia (1)  ·  Ukraine (1)  ·  United Kingdom (1)

Top investigators

Angela Smith, MD (1)  ·  Cristina Bulai Livideanu, MD, MSc (1)  ·  Nanja Van Geel, Pr (1)  ·  Olivier Lortholary, MD, PhD (1)  ·  Weizhong Jiang, MD (1)

Results publications

PMID 28069279, PMID 36048877

NIH funding

2016 (1)