nitisinone: Clinical Trials

4 trials of nitisinone, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

4 completed. 4 Phase 2, 1 Phase 1, 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 24Completed 4
Phase 11Completed 1
Phase 31Completed 1

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Trials (filtered) newest first · largest first

All 4 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Dose Response Study of Nitisinone in Alkaptonuria
Nitisinone - Alkaptonuria
Phase 2CompletedUniversity of Liverpool402013-05-012014-06-11
Nitisinone for Type 1B Oculocutaneous Albinism
Nitisinone - Albinism, Vision Loss
Phase 1 / Phase 2CompletedNational Eye Institute (NEI)52013-04-162019-02-26
Nitisinone (NTBC) In Different Age Groups Of Patients With Alkaptonuria
Nitisinone - Alkaptonuria
Phase 2 / Phase 3CompletedUniversity of California, San Diego82011-01-012021-04-22
Long-Term Study of Nitisinone to Treat Alkaptonuria
Nitisinone (NTBC) - Alkaptonuria
Phase 2CompletedNational Human Genome Research Institute (NHGRI)402005-01-012021-08-26

Conditions studied

Alkaptonuria (3)  ·  Albinism (1)  ·  Arthritis (1)  ·  Corneal Injuries (1)  ·  Photophobia (1)  ·  Vision Disorders (1)

Sponsors

National Eye Institute (NEI) (1)  ·  National Human Genome Research Institute (NHGRI) (1)  ·  University of California, San Diego (1)  ·  University of Liverpool (1)

Countries

United States (3)  ·  United Kingdom (1)

Top investigators

Brian P Brooks, M.D. (1)  ·  L Ranganath (1)  ·  William L Nyhan, MD, PhD (1)

Results publications

PMID 25475116, PMID 25665838, PMID 30674731, PMID 31296884