1 recruiting. 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 3 | 1 | Recruiting 1 |
Follow nexiguran ziclumeran: new trials by email Literature Review of nexiguran ziclumeran trials Research Report on nexiguran ziclumeran
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Phase 3 Study of NTLA-2001 in ATTRv-PN nexiguran ziclumeran, Normal Saline as Placebo - Neuromuscular Disease, Neuromuscular Diseases (NMD) | Phase 3 | Recruiting | Intellia Therapeutics | 60 | 2024-11-22 | 2026-04-16 |
Amyloid Neuropathies (1) · Amyloid Neuropathies, Familial (1) · Amyloidosis (1) · Amyloidosis, Familial (1) · Amyloidosis, Hereditary, Transthyretin-Related (1) · Genetic Diseases, Inborn (1) · Heredodegenerative Disorders, Nervous System (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1) · Nervous System Diseases (1) · Neurodegenerative Diseases (1) · Neuromuscular Diseases (1) · Peripheral Nervous System Diseases (1) · Polyneuropathies (1)
Argentina (1) · Brazil (1) · Mexico (1) · Singapore (1) · Taiwan (1) · Thailand (1)