nexiguran ziclumeran: Clinical Trials

1 trial of nexiguran ziclumeran, newest first

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1 recruiting. 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 31Recruiting 1

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Trials newest first · largest first

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TrialPhaseStatusSponsorEnrollmentStartUpdated
A Phase 3 Study of NTLA-2001 in ATTRv-PN
nexiguran ziclumeran, Normal Saline as Placebo - Neuromuscular Disease, Neuromuscular Diseases (NMD)
Phase 3RecruitingIntellia Therapeutics602024-11-222026-04-16

Conditions studied

Amyloid Neuropathies (1)  ·  Amyloid Neuropathies, Familial (1)  ·  Amyloidosis (1)  ·  Amyloidosis, Familial (1)  ·  Amyloidosis, Hereditary, Transthyretin-Related (1)  ·  Genetic Diseases, Inborn (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Nervous System Diseases (1)  ·  Neurodegenerative Diseases (1)  ·  Neuromuscular Diseases (1)  ·  Peripheral Nervous System Diseases (1)  ·  Polyneuropathies (1)

Sponsors

Intellia Therapeutics (1)

Countries

Argentina (1)  ·  Brazil (1)  ·  Mexico (1)  ·  Singapore (1)  ·  Taiwan (1)  ·  Thailand (1)