Xlsma: Clinical Trials

1 trial for Xlsma, newest first

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1 withdrawn. .

Follow Xlsma: new trials by email Literature Review of Xlsma trials Research Report on Xlsma

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Multi-center Clinical Study on the Diagnosis and Treatment Management of Rare Neurological Disease in Children
Xlsma, DMD
WithdrawnChildren's Hospital of Fudan University2021-09-302021-08-11

Narrower conditions

Adrenoleukodystrophy (1)  ·  Arthrogryposis multiplex congenita, distal, X-linked (1)

Broader conditions

Adrenal Gland Diseases (1)  ·  Adrenal Insufficiency (1)  ·  Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Central Nervous System Diseases (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Demyelinating Diseases (1)  ·  Endocrine System Diseases (1)  ·  Genetic Diseases, Inborn (1)  ·  Genetic Diseases, X-Linked (1)  ·  Hereditary Central Nervous System Demyelinating Diseases (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Intellectual Disability (1)  ·  Leukoencephalopathies (1)

Sponsors

Children's Hospital of Fudan University (1)

Countries

China (1)