1 withdrawn. .
Follow Xlsma: new trials by email Literature Review of Xlsma trials Research Report on Xlsma
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Multi-center Clinical Study on the Diagnosis and Treatment Management of Rare Neurological Disease in Children Xlsma, DMD | Withdrawn | Children's Hospital of Fudan University | 2021-09-30 | 2021-08-11 |
Adrenoleukodystrophy (1) · Arthrogryposis multiplex congenita, distal, X-linked (1)
Adrenal Gland Diseases (1) · Adrenal Insufficiency (1) · Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Central Nervous System Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Demyelinating Diseases (1) · Endocrine System Diseases (1) · Genetic Diseases, Inborn (1) · Genetic Diseases, X-Linked (1) · Hereditary Central Nervous System Demyelinating Diseases (1) · Heredodegenerative Disorders, Nervous System (1) · Intellectual Disability (1) · Leukoencephalopathies (1)
Children's Hospital of Fudan University (1)
China (1)