Vitelliform Macular Dystrophy: Clinical Trials

1 trial for Vitelliform Macular Dystrophy, newest first

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1 recruiting. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Recruiting 1
Phase 21Recruiting 1

Follow Vitelliform Macular Dystrophy: new trials by email Literature Review of Vitelliform Macular Dystrophy trials Research Report on Vitelliform Macular Dystrophy

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Safety and Tolerability of Subretinally Injected OPGx-BEST1 in Patients With Best Vitelliform Macular Dystrophy (BVMD) or Autosomal-Recessive Bestrophinopathy (ARB)
OPGx-BEST1 - ARB, BVMD
Phase 1 / Phase 2RecruitingOpus Genetics, Inc102025-09-252026-09-24

Narrower conditions

Bestrophinopathy (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Eye Diseases (1)  ·  Eye Diseases, Hereditary (1)  ·  Genetic Diseases, Inborn (1)  ·  Macular Degeneration (1)  ·  Retinal Degeneration (1)  ·  Retinal Diseases (1)

Sponsors

Opus Genetics, Inc (1)

Countries

United States (1)