2 terminated, 1 withdrawn. 3 Phase 2, 1 Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 3 | Terminated 2, Withdrawn 1 |
| Phase 1 | 1 | Terminated 1 |
Follow Urea Cycle Disorder: new trials by email Literature Review of Urea Cycle Disorder trials Research Report on Urea Cycle Disorder
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| UNLOCKED: A Phase 2, Open-label Trial With KB195 in Subjects With a Urea Cycle Disorder KB195 - Urea Cycle Disorder | Phase 2 | Terminated | Kaleido Biosciences | 13 | 2019-09-17 | 2022-01-25 |
| A Safety and Efficacy Study of Infusions of HepaStem in Urea Cycle Disorders Pediatric Patients HepaStem Infusion - Urea Cycle Disorder | Phase 2 | Withdrawn | HLB Cell Co., Ltd. | 2018-07-12 | 2020-11-06 | |
| Manipulating the Gut Microbiome Study Acetohydroxamic Acid Oral Tablet, No treatment - Urea Cycle Disorder | Phase 1 / Phase 2 | Terminated | Nicholas Ah Mew | 4 | 2017-03-24 | 2021-12-15 |
Urea Cycle Disorders, Inborn (3) · Ornithine Carbamoyltransferase Deficiency Disease (2) · Hyperammonemia (1)
Amino Acid Metabolism, Inborn Errors (3) · Brain Diseases (3) · Brain Diseases, Metabolic (3) · Brain Diseases, Metabolic, Inborn (3) · Central Nervous System Diseases (3) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3) · Genetic Diseases, Inborn (3) · Metabolic Diseases (3) · Metabolism, Inborn Errors (3) · Nervous System Diseases (3) · Nutritional and Metabolic Diseases (3) · Genetic Diseases, X-Linked (2) · Pathologic Processes (1) · Pathological Conditions, Signs and Symptoms (1)
HLB Cell Co., Ltd. (1) · Kaleido Biosciences (1) · Nicholas Ah Mew (1)
United States (2) · Belgium (1) · Germany (1) · South Korea (1) · Spain (1) · Switzerland (1) · Turkey (Türkiye) (1) · United Kingdom (1)
Mark Wingertzahn, PhD (1) · Nicholas Ah Mew, MD (1) · Sanghoon Lee, MD. Ph.D (1)