Telomere Disease: Clinical Trials

5 trials for Telomere Disease, newest first

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1 active not recruiting, 1 completed, 1 recruiting, 1 terminated. 2 Phase 2, 1 Not applicable, 1 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 22Completed 1, Terminated 1
Not applicable1Unknown 1
Phase 11Recruiting 1

Follow Telomere Disease: new trials by email Literature Review of Telomere Disease trials Research Report on Telomere Disease

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Quercetin Dyskeratosis Congenita (DC)/Telomere Biology Disorders (TBD)
Quercetin - Dyskeratosis Congenita, Telomere Disease
Phase 1RecruitingChildren's Hospital Medical Center, Cincinnati122026-05-292026-09-10
Hereditary Influences on Pulmonary Fibrosis Trajectories
Interstitial Lung Disease Due to Systemic Disease (Telomere Biology Disorder), Idiopathic Pulmonary Fibrosis (IPF)
Active not recruitingIstituto Clinico Humanitas2502026-04-012026-05-12
Nasal Brushing for the Diagnosis and Understanding of Telomeropathies
Nasal brushing, Sniffin' Sticks - Telomere Disease, Telomere Shortening
Not applicableUnknownCliniques universitaires Saint-Luc- Université Catholique de Louvain2502022-10-012022-11-04
The TELO-SCOPE Study: Attenuating Telomere Attrition With Danazol. Is There Scope to Dramatically Improve Health Outcomes for Adults and Children With Pulmonary Fibrosis
Danazol, Placebo - Pulmonary Fibrosis, Telomere Shortening
Phase 2TerminatedThe University of Queensland292021-09-072025-08-05
Low-Dose Danazol for the Treatment of Telomere Related Diseases
Danazol - Telomere Disease
Phase 2CompletedNational Heart, Lung, and Blood Institute (NHLBI)182018-02-082026-06-25

Narrower conditions

Dyskeratosis Congenita (2)  ·  Pulmonary Fibrosis (2)  ·  Anemia, Aplastic (1)  ·  Anosmia (1)  ·  Idiopathic Pulmonary Fibrosis (1)  ·  Liver Cirrhosis (1)  ·  Lung Diseases, Interstitial (1)

Broader conditions

Bone Marrow Diseases (3)  ·  Bone Marrow Failure Disorders (3)  ·  Hematologic Diseases (3)  ·  Hemic and Lymphatic Diseases (3)  ·  Lung Diseases (3)  ·  Pathological Conditions, Signs and Symptoms (3)  ·  Respiratory Tract Diseases (3)  ·  Congenital Abnormalities (2)  ·  Congenital Bone Marrow Failure Syndromes (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Fibrosis (2)  ·  Genetic Diseases, Inborn (2)  ·  Genetic Diseases, X-Linked (2)  ·  Lung Diseases, Interstitial (2)  ·  Pathologic Processes (2)

Interventions

Danazol (2)  ·  Quercetin (1)

Sponsors

Children's Hospital Medical Center, Cincinnati (1)  ·  Cliniques universitaires Saint-Luc- Université Catholique de Louvain (1)  ·  Istituto Clinico Humanitas (1)  ·  National Heart, Lung, and Blood Institute (NHLBI) (1)  ·  The University of Queensland (1)

Countries

United States (2)  ·  Australia (1)  ·  Belgium (1)  ·  Italy (1)

Top investigators

Caroline Huart, MD, PhD (1)  ·  Emma M Groarke, M.D. (1)  ·  Francesco Amati, MD (1)  ·  Parinda Mehta, MD (1)

Results publications

PMID 34857525