2 recruiting, 1 completed, 1 unknown. 1 Not applicable, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Not applicable | 1 | Recruiting 1 |
| Phase 2 | 1 | Completed 1 |
Follow Spinal Muscular Atrophy, Type IV: new trials by email Literature Review of Spinal Muscular Atrophy, Type IV trials Research Report on Spinal Muscular Atrophy, Type IV
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Long Read Analysis in Spinal Muscular Atrophy - LOREASI blood sample - Spinal Muscular Atrophy (SMA) | Not applicable | Recruiting | University Hospital, Rouen | 27 | 2025-05-15 | 2026-01-12 |
| Advanced Multi-omics and -System Approaches to Identify Novel Biomarkers for SMA Spinal Muscular Atrophy (SMA) | Recruiting | Istituto Giannina Gaslini | 200 | 2025-02-05 | 2026-10-20 | |
| Longitudinal Data Collection in Pediatric and Adult Patients With Spinal Muscular Atrophy in Latin America Spinal Muscular Atrophy | Unknown | Hospital Israelita Albert Einstein | 361 | 2022-08-17 | 2024-03-08 | |
| SPACE Trial: Pyridostigmine vs Placebo in SMA Types 2, 3 and 4 Pyridostigmine, Placebo - Spinal Muscular Atrophy, SMA | Phase 2 | Completed | UMC Utrecht | 39 | 2015-12-01 | 2018-02-05 |
Muscular Atrophy, Spinal (4) · Spinal Muscular Atrophies of Childhood (2) · Spinal muscular atrophy 4 (1)
Central Nervous System Diseases (4) · Motor Neuron Disease (4) · Nervous System Diseases (4) · Neurodegenerative Diseases (4) · Neuromuscular Diseases (4) · Spinal Cord Diseases (4) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Genetic Diseases, Inborn (2) · Heredodegenerative Disorders, Nervous System (2)
Blood Specimen Collection (1) · Pyridostigmine Bromide (1)
Hospital Israelita Albert Einstein (1) · Istituto Giannina Gaslini (1) · UMC Utrecht (1) · University Hospital, Rouen (1)
Argentina (1) · Brazil (1) · Chile (1) · Colombia (1) · France (1) · Italy (1) · Mexico (1) · Netherlands (1) · Uruguay (1)
Henrique Fonseca, PhD (1) · W.L. Van der Pol, MD, PhD (1)