Sickle-Cell Disease With Crisis: Clinical Trials

1 trial for Sickle-Cell Disease With Crisis, newest first

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1 recruiting. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Recruiting 1
Phase 21Recruiting 1

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Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Investigation Into the Use of BAH243 Lentiviral Vector for Gene Therapy in Treating Sickle Cell Disease
Drug Product is administered by IV infusion following myeloablative conditioning with busulfan - Sickle Cell Disease, Sickle-Cell Disease With Crisis
Phase 1 / Phase 2RecruitingEssen Biotech852024-08-012024-11-05

Narrower conditions

Anemia, Sickle Cell (1)  ·  Vaso-Occlusive Crises (1)

Broader conditions

Anemia (1)  ·  Anemia, Hemolytic (1)  ·  Anemia, Hemolytic, Congenital (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Hematologic Diseases (1)  ·  Hemic and Lymphatic Diseases (1)  ·  Hemoglobinopathies (1)

Interventions

Busulfan (1)

Sponsors

Essen Biotech (1)

Countries

China (1)