Rett Syndrome: Clinical Trials

1 trial for Rett Syndrome, newest first

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1 withdrawn. 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 21Withdrawn 1

Follow Rett Syndrome: new trials by email Literature Review of Rett Syndrome trials Research Report on Rett Syndrome

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
An Exploratory Open Label Study of EPI-743 (Vincerinone TM) in Children With Autism Spectrum Disorder
EPI-743 - Autism Spectrum Disorder
Phase 2WithdrawnEdison Pharmaceuticals Inc2014-10-312022-01-21

Narrower conditions

Angelman Syndrome (1)  ·  Autism Spectrum Disorder (1)  ·  Autistic Disorder (1)  ·  Mitochondrial Diseases (1)

Broader conditions

Abnormalities, Multiple (1)  ·  Central Nervous System Diseases (1)  ·  Child Development Disorders, Pervasive (1)  ·  Chromosome Disorders (1)  ·  Congenital Abnormalities (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Genetic Diseases, X-Linked (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Imprinting Disorders (1)  ·  Intellectual Disability (1)  ·  Mental Disorders (1)  ·  Metabolic Diseases (1)  ·  Movement Disorders (1)  ·  Nervous System Diseases (1)

Interventions

alpha-tocotrienol quinone (1)

Sponsors

Edison Pharmaceuticals Inc (1)