Pyruvate Metabolism, Inborn Errors: Clinical Trials

1 trial for Pyruvate Metabolism, Inborn Errors, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

1 completed. 1 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 11Completed 1

Follow Pyruvate Metabolism, Inborn Errors: new trials by email Literature Review of Pyruvate Metabolism, Inborn Errors trials Research Report on Pyruvate Metabolism, Inborn Errors

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Dose-escalating Clinical Trial With KH176
KH176, placebo - MELAS, LHON
Phase 1CompletedKhondrion BV322015-05-012021-10-18

Narrower conditions

Leigh Disease (1)  ·  MELAS Syndrome (1)  ·  Mitochondrial Diseases (1)

Broader conditions

Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Carbohydrate Metabolism, Inborn Errors (1)  ·  Cardiovascular Diseases (1)  ·  Central Nervous System Diseases (1)  ·  Cerebral Small Vessel Diseases (1)  ·  Cerebrovascular Disorders (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Mitochondrial Encephalomyopathies (1)  ·  Mitochondrial Myopathies (1)  ·  Muscular Diseases (1)

Interventions

6-hydroxy-2,5,7,8-tetramethylchroman-2-carboxylic acid (1)

Sponsors

Khondrion BV (1)

Countries

Belgium (1)

Results publications

PMID 29037240