1 completed, 1 terminated. .
Follow Pyruvate Kinase Deficiency Anemia: new trials by email Literature Review of Pyruvate Kinase Deficiency Anemia trials Research Report on Pyruvate Kinase Deficiency Anemia
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Acquired Pyruvate Kinase Deficiency In Clonal Myeloid Neoplasms Blood Draw - Pyruvate Kinase Deficiency, Pyruvate Kinase Deficiency Anemia | Completed | Massachusetts General Hospital | 18 | 2022-02-01 | 2026-05-19 | |
| Pyruvate Kinase (PK) Deficiency Global Longitudinal Registry: Patient-Reported Outcomes (PRO) Pyruvate Kinase Deficiency, Pyruvate Kinase Deficiency Anemia | Terminated | Agios Pharmaceuticals, Inc. | 15 | 2021-07-02 | 2023-09-07 |
Pyruvate Kinase Deficiency of Red Cells (2) · Anemia (1) · Anemia, Hemolytic (1) · Anemia, Hemolytic, Congenital (1) · Anemia, Hemolytic, Congenital Nonspherocytic (1) · Leukemia, Myeloid, Acute (1) · Myelodysplastic Syndromes (1) · Myelodysplastic-Myeloproliferative Diseases (1) · Myeloproliferative Disorders (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Genetic Diseases, Inborn (2) · Hematologic Diseases (2) · Hemic and Lymphatic Diseases (2) · Anemia (1) · Anemia, Hemolytic (1) · Anemia, Hemolytic, Congenital (1) · Bone Marrow Diseases (1) · Leukemia (1) · Leukemia, Myeloid (1) · Neoplasms (1) · Neoplasms by Histologic Type (1)
Agios Pharmaceuticals, Inc. (1) · Massachusetts General Hospital (1)
United States (2) · Italy (1) · Netherlands (1) · Spain (1) · United Kingdom (1)