Pyruvate Kinase Deficiency Anemia: Clinical Trials

2 trials for Pyruvate Kinase Deficiency Anemia, newest first

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1 completed, 1 terminated. .

Follow Pyruvate Kinase Deficiency Anemia: new trials by email Literature Review of Pyruvate Kinase Deficiency Anemia trials Research Report on Pyruvate Kinase Deficiency Anemia

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Acquired Pyruvate Kinase Deficiency In Clonal Myeloid Neoplasms
Blood Draw - Pyruvate Kinase Deficiency, Pyruvate Kinase Deficiency Anemia
CompletedMassachusetts General Hospital182022-02-012026-05-19
Pyruvate Kinase (PK) Deficiency Global Longitudinal Registry: Patient-Reported Outcomes (PRO)
Pyruvate Kinase Deficiency, Pyruvate Kinase Deficiency Anemia
TerminatedAgios Pharmaceuticals, Inc.152021-07-022023-09-07

Narrower conditions

Pyruvate Kinase Deficiency of Red Cells (2)  ·  Anemia (1)  ·  Anemia, Hemolytic (1)  ·  Anemia, Hemolytic, Congenital (1)  ·  Anemia, Hemolytic, Congenital Nonspherocytic (1)  ·  Leukemia, Myeloid, Acute (1)  ·  Myelodysplastic Syndromes (1)  ·  Myelodysplastic-Myeloproliferative Diseases (1)  ·  Myeloproliferative Disorders (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Genetic Diseases, Inborn (2)  ·  Hematologic Diseases (2)  ·  Hemic and Lymphatic Diseases (2)  ·  Anemia (1)  ·  Anemia, Hemolytic (1)  ·  Anemia, Hemolytic, Congenital (1)  ·  Bone Marrow Diseases (1)  ·  Leukemia (1)  ·  Leukemia, Myeloid (1)  ·  Neoplasms (1)  ·  Neoplasms by Histologic Type (1)

Interventions

Blood Specimen Collection (1)

Sponsors

Agios Pharmaceuticals, Inc. (1)  ·  Massachusetts General Hospital (1)

Countries

United States (2)  ·  Italy (1)  ·  Netherlands (1)  ·  Spain (1)  ·  United Kingdom (1)

Top investigators

Hanny Al-Samkari, MD (1)