NF1: Clinical Trials

2 trials for NF1, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

2 recruiting. 2 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 12Recruiting 2
Phase 21Recruiting 1

Follow NF1: new trials by email Literature Review of NF1 trials Research Report on NF1

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Feasibility and Tolerability of IMLYGIC for the Treatment of Cutaneous Neurofibromas in Adults With NF1
Imlygic - NF1, Neurofibromatosis
Phase 1RecruitingJohns Hopkins University102026-02-012026-05-08
Mirdametinib Monotherapy in Adults With Neurofibromatosis 1 (NF1) and Cutaneous Neurofibromas (cNF).
Mirdametinib - NF1, Cutaneous Neurofibroma
Phase 1 / Phase 2RecruitingJohns Hopkins University242024-02-122026-04-13

Narrower conditions

Neurofibroma (1)  ·  Neurofibromatoses (1)  ·  Neurofibromatosis 1 (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Neoplasms (1)  ·  Neoplasms by Histologic Type (1)  ·  Neoplasms, Nerve Tissue (1)  ·  Neoplastic Syndromes, Hereditary (1)  ·  Nerve Sheath Neoplasms (1)  ·  Nervous System Diseases (1)  ·  Nervous System Neoplasms (1)  ·  Neurocutaneous Syndromes (1)  ·  Neurodegenerative Diseases (1)  ·  Neuromuscular Diseases (1)  ·  Peripheral Nervous System Diseases (1)  ·  Peripheral Nervous System Neoplasms (1)

Interventions

mirdametinib (1)  ·  talimogene laherparepvec (1)

Sponsors

Johns Hopkins University (2)

Countries

United States (2)

Top investigators

Carlos Romo, MD (2)