Neuroferritinopathy: Clinical Trials

1 trial for Neuroferritinopathy, newest first

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1 recruiting. .

Follow Neuroferritinopathy: new trials by email Literature Review of Neuroferritinopathy trials Research Report on Neuroferritinopathy

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
TIRCON International NBIA Registry
Neurodegeneration With Brain Iron Accumulation (NBIA), Pantothenate Kinase-associated Neurodegeneration (PKAN)
RecruitingLMU Klinikum20002012-06-142025-06-05

Narrower conditions

Familial apoceruloplasmin deficiency (1)  ·  Fatty Acid Hydroxylase-Associated Neurodegeneration (1)  ·  Kufor-Rakeb syndrome (1)  ·  Neuroaxonal Dystrophies (1)  ·  Pantothenate Kinase-Associated Neurodegeneration (1)  ·  Woodhouse Sakati syndrome (1)

Broader conditions

Basal Ganglia Diseases (1)  ·  Brain Diseases (1)  ·  Central Nervous System Diseases (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Movement Disorders (1)  ·  Nervous System Diseases (1)  ·  Neurodegenerative Diseases (1)

Sponsors

LMU Klinikum (1)

Countries

Canada (1)  ·  Czechia (1)  ·  Germany (1)  ·  Italy (1)  ·  Netherlands (1)  ·  Poland (1)  ·  Serbia (1)  ·  Spain (1)

Top investigators

Thomas Klopstock, Prof. Dr. (1)