Multiple Endocrine Neoplasia Type 2b: Clinical Trials

5 trials for Multiple Endocrine Neoplasia Type 2b, newest first

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2 completed, 1 active not recruiting, 1 recruiting, 1 withdrawn. 2 Phase 1, 2 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 12Completed 1, Withdrawn 1
Phase 22Completed 2

Follow Multiple Endocrine Neoplasia Type 2b: new trials by email Literature Review of Multiple Endocrine Neoplasia Type 2b trials Research Report on Multiple Endocrine Neoplasia Type 2b

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Early Check: Expanded Screening in Newborns
Confirmatory Testing - Spinal Muscular Atrophy, Fragile X Syndrome
Active not recruitingRTI International300002018-10-152026-07-01
Veliparib, Capecitabine, and Temozolomide in Patients With Advanced, Metastatic, and Recurrent Neuroendocrine Tumor
Capecitabine, Temozolomide, Veliparib - Functional Pancreatic Neuroendocrine Tumor, Malignant Somatostatinoma
Phase 1WithdrawnVanderbilt-Ingram Cancer Center2017-12-012017-09-28
Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
Rare Disorders, Undiagnosed Disorders
RecruitingSanford Health200002010-07-012025-05-29
Vandetanib to Treat Children and Adolescents With Medullary Thyroid Cancer
Vandetanib - Medullary Thyroid Carcinoma, Multiple Endocrine Neoplasia Type 2A
Phase 1 / Phase 2CompletedNational Cancer Institute (NCI)172007-07-202020-12-22
Sorafenib Tosylate in Treating Patients With Metastatic, Locally Advanced, or Recurrent Medullary Thyroid Cancer
Sorafenib Tosylate - Hereditary Thyroid Gland Medullary Carcinoma, Locally Advanced Thyroid Gland Medullary Carcinoma
Phase 2CompletedNational Cancer Institute (NCI)212006-11-032024-02-06

Narrower conditions

Multiple Endocrine Neoplasia Type 2a (4)  ·  Carcinoma, Medullary (3)  ·  Ataxia with vitamin E deficiency (2)  ·  Cystinosis (2)  ·  Hyperargininemia (2)  ·  Hypophosphatasia (2)  ·  Leukodystrophy, Metachromatic (2)  ·  Multiple Endocrine Neoplasia (2)  ·  Multiple Endocrine Neoplasia Type 1 (2)  ·  Pitt-Hopkins syndrome (2)  ·  Stickler syndrome, type 1 (2)  ·  Stickler syndrome, type 2 (2)  ·  3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency (1)  ·  3-Hydroxyacyl-CoA Dehydrogenase Deficiency (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (5)  ·  Endocrine Gland Neoplasms (5)  ·  Endocrine System Diseases (5)  ·  Genetic Diseases, Inborn (5)  ·  Neoplasms (5)  ·  Neoplasms by Histologic Type (5)  ·  Neoplasms by Site (5)  ·  Neoplasms, Multiple Primary (5)  ·  Neoplastic Syndromes, Hereditary (5)  ·  Neoplasms, Germ Cell and Embryonal (4)  ·  Neoplasms, Glandular and Epithelial (4)  ·  Neoplasms, Nerve Tissue (4)  ·  Neuroectodermal Tumors (4)  ·  Adenocarcinoma (3)  ·  Carcinoma (3)

Interventions

Capecitabine (1)  ·  Sorafenib (1)  ·  Temozolomide (1)  ·  vandetanib (1)  ·  veliparib (1)

Sponsors

National Cancer Institute (NCI) (2)  ·  RTI International (1)  ·  Sanford Health (1)  ·  Vanderbilt-Ingram Cancer Center (1)

Countries

United States (4)  ·  Australia (1)

Top investigators

Bhavana Konda (1)  ·  Brigitte C Widemann, M.D. (1)  ·  Curt Scharfe, MD, PhD (1)  ·  Jordan Berlin, M.D. (1)

Results publications

PMID 23766359, PMID 24617713, PMID 25972901, PMID 29187393, PMID 31315600, PMID 35142618

NIH funding

N01CM00070 (1), N01CM62207 (1), P30CA016058 (1)