2 completed, 2 terminated. 4 Phase 3, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 3 | 4 | Completed 2, Terminated 2 |
| Phase 2 | 1 | Terminated 1 |
Follow Mucopolysaccharidosis VI: new trials by email Literature Review of Mucopolysaccharidosis VI trials Research Report on Mucopolysaccharidosis VI
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Clinical Trial of Growth Hormone in MPS I, II, and VI Somatropin (DNA origin) - Mucopolysaccharidosis I, Mucopolysaccharidosis II | Phase 2 / Phase 3 | Terminated | Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center | 2 | 2008-11-01 | 2018-09-05 |
| ALD-101 Adjuvant Therapy of Unrelated Umbilical Cord Blood Transfusion (UCBT) in Patients With Inherited Metabolic Diseases ALD-101 - Inherited Metabolic Diseases, Lysosomal Storage Disorders | Phase 3 | Terminated | Aldagen | 40 | 2008-03-01 | 2014-07-08 |
| Study of rhASB in Patients With Mucopolysaccharidosis VI N-acetylgalactosamine 4-sulfatase, Placebo/rhASB - Mucopolysaccharidosis VI | Phase 3 | Completed | BioMarin Pharmaceutical | 39 | 2004-02-01 | 2010-02-02 |
| Study of Recombinant Human N-acetylgalactosamine 4-sulfatase (rhASB) in Patients With MPS VI Placebo, N-acetylgalactosamine 4-sulfatase - Mucopolysaccharidosis VI | Phase 3 | Completed | BioMarin Pharmaceutical | 39 | 2003-09-01 | 2009-12-24 |
Mucopolysaccharidosis I (2) · Mucopolysaccharidosis II (2) · Sudden Infant Death (2) · Adrenoleukodystrophy (1) · Canavan Disease (1) · Dwarfism (1) · Fucosidosis (1) · Gangliosidosis, GM1 (1) · Leukodystrophy, Globoid Cell (1) · Leukodystrophy, Metachromatic (1) · Lysosomal Storage Diseases (1) · Metabolism, Inborn Errors (1) · Mucolipidoses (1) · Mucopolysaccharidoses (1)
Carbohydrate Metabolism, Inborn Errors (4) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (4) · Connective Tissue Diseases (4) · Genetic Diseases, Inborn (4) · Metabolic Diseases (4) · Mucinoses (4) · Nutritional and Metabolic Diseases (4) · Skin and Connective Tissue Diseases (4) · Lysosomal Storage Diseases (3) · Metabolism, Inborn Errors (3) · Mucopolysaccharidoses (3) · Bone Diseases (2) · Death (2) · Death, Sudden (2) · Endocrine System Diseases (2)
N-Acetylgalactosamine-4-Sulfatase (2) · Growth Hormone (1) · Human Growth Hormone (1)
BioMarin Pharmaceutical (2) · Aldagen (1) · Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center (1)
United States (4)
James Hinson, MD (1) · Joanne Kurtzberg, MD (1) · Lynda E Polgreen, M.D. (1)