Mucinoses: Clinical Trials

1 trial for Mucinoses, newest first

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1 withdrawn. 1 Phase 4.

By phase and status

PhaseTrialsStatus
Phase 41Withdrawn 1

Follow Mucinoses: new trials by email Literature Review of Mucinoses trials Research Report on Mucinoses

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Study of ELAPRASE in Treatment-naïve Participants With Hunter Syndrome (Mucopolysaccharidosis [MPS] II)
ELAPRASE, Rituximab, Methotrexate - Mucopolysaccharidosis (MPS), Hunter Syndrome
Phase 4WithdrawnTakeda2023-02-282025-12-09

Narrower conditions

Mucopolysaccharidoses (1)  ·  Mucopolysaccharidosis II (1)

Broader conditions

Carbohydrate Metabolism, Inborn Errors (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Connective Tissue Diseases (1)  ·  Genetic Diseases, Inborn (1)  ·  Genetic Diseases, X-Linked (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Intellectual Disability (1)  ·  Lysosomal Storage Diseases (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Nervous System Diseases (1)  ·  Neurobehavioral Manifestations (1)  ·  Neurologic Manifestations (1)  ·  Nutritional and Metabolic Diseases (1)

Interventions

Immunoglobulins, Intravenous (1)  ·  Methotrexate (1)  ·  Rituximab (1)  ·  idursulfase (1)

Sponsors

Takeda (1)

Countries

United States (1)