1 completed. 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 1 | Completed 1 |
Follow Mevalonate Kinase Deficiency: new trials by email Literature Review of Mevalonate Kinase Deficiency trials Research Report on Mevalonate Kinase Deficiency
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Canakinumab in Patients With Active Hyper-IgD Syndrome Canakinumab - Mevalonate Kinase Deficiency | Phase 2 | Completed | Novartis Pharmaceuticals | 9 | 2011-03-01 | 2015-11-05 |
Blood Protein Disorders (1) · Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Central Nervous System Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Hematologic Diseases (1) · Hemic and Lymphatic Diseases (1) · Hereditary Autoinflammatory Diseases (1) · Hypergammaglobulinemia (1) · Immune System Diseases (1) · Immunoproliferative Disorders (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1)
canakinumab (1)
Spain (1)