Mevalonate Kinase Deficiency: Clinical Trials

1 trial for Mevalonate Kinase Deficiency, newest first

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1 completed. 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 21Completed 1

Follow Mevalonate Kinase Deficiency: new trials by email Literature Review of Mevalonate Kinase Deficiency trials Research Report on Mevalonate Kinase Deficiency

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Canakinumab in Patients With Active Hyper-IgD Syndrome
Canakinumab - Mevalonate Kinase Deficiency
Phase 2CompletedNovartis Pharmaceuticals92011-03-012015-11-05

Broader conditions

Blood Protein Disorders (1)  ·  Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Central Nervous System Diseases (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Hematologic Diseases (1)  ·  Hemic and Lymphatic Diseases (1)  ·  Hereditary Autoinflammatory Diseases (1)  ·  Hypergammaglobulinemia (1)  ·  Immune System Diseases (1)  ·  Immunoproliferative Disorders (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)

Interventions

canakinumab (1)

Sponsors

Novartis Pharmaceuticals (1)

Countries

Spain (1)

Results publications

PMID 28482144