2 recruiting. 2 Phase 1, 2 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 2 | Recruiting 2 |
| Phase 2 | 2 | Recruiting 2 |
Follow Metabolic Disorders: new trials by email Literature Review of Metabolic Disorders trials Research Report on Metabolic Disorders
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Reduced Intensity Conditioning and Familial HLA-Mismatched BMT for Non-Malignant Disorders RIC regimen, GVHD prophylaxis regimen - Severe Sickle Cell Disease, Bone Marrow Failure Syndromes | Phase 1 / Phase 2 | Recruiting | Washington University School of Medicine | 29 | 2017-03-20 | 2026-05-29 |
| Campath/Fludarabine/Melphalan Transplant Conditioning for Non-Malignant Diseases Treatment Plan 1: Stratum 1, Treatment Plan 2: Strata 2, 3, or 4, GVHD Regimen A: UCB Recipients - Metabolic Disorders, Hematologic, Immune, or Bone Marrow Disorders | Phase 1 / Phase 2 | Recruiting | Washington University School of Medicine | 220 | 2001-12-01 | 2026-09-16 |
Hemoglobinopathies (2) · Metabolic Diseases (2) · Anemia, Sickle Cell (1) · Bone Marrow Failure Disorders (1) · Immune System Diseases (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Genetic Diseases, Inborn (2) · Hematologic Diseases (2) · Hemic and Lymphatic Diseases (2) · Nutritional and Metabolic Diseases (2) · Anemia (1) · Anemia, Hemolytic (1) · Anemia, Hemolytic, Congenital (1) · Bone Marrow Diseases (1)
Washington University School of Medicine (2)
United States (2) · Canada (1)
PMID 15592491, PMID 16990602, PMID 18026148, PMID 18500373, PMID 26348869, PMID 32813873