1 terminated. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Terminated 1 |
| Phase 2 | 1 | Terminated 1 |
Follow Leukodystrophy, Metachromatic: new trials by email Literature Review of Leukodystrophy, Metachromatic trials Research Report on Leukodystrophy, Metachromatic
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Phase I/II Pilot Study of Mixed Chimerism to Treat Inherited Metabolic Disorders hematopoietic stem cell infusion - Hurler Syndrome (MPS I), Hurler-Scheie Syndrome | Phase 1 / Phase 2 | Terminated | Talaris Therapeutics Inc. | 3 | 2011-04-01 | 2023-04-12 |
Adrenoleukodystrophy (1) · Leukodystrophy, Globoid Cell (1) · Mucopolysaccharidosis I (1) · Mucopolysaccharidosis II (1) · Mucopolysaccharidosis III (1) · Niemann-Pick Diseases (1) · Sandhoff Disease (1) · Sudden Infant Death (1) · Tay-Sachs Disease (1) · alpha-Mannosidosis (1)
Adrenal Gland Diseases (1) · Adrenal Insufficiency (1) · Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Carbohydrate Metabolism, Inborn Errors (1) · Central Nervous System Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Connective Tissue Diseases (1) · Death (1) · Death, Sudden (1) · Demyelinating Diseases (1) · Endocrine System Diseases (1) · Gangliosidoses (1) · Gangliosidoses, GM2 (1)
United States (1)