2 active not recruiting. 2 Phase 2, 1 Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 2 | Active not recruiting 2 |
| Phase 1 | 1 | Active not recruiting 1 |
Follow Leukodystrophy, Globoid Cell: new trials by email Literature Review of Leukodystrophy, Globoid Cell trials Research Report on Leukodystrophy, Globoid Cell
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Gene Transfer Clinical Trial for Infantile and Late Infantile Krabbe Disease Treated Previously With HSCT FBX-101 - Krabbe Disease | Phase 1 / Phase 2 | Active not recruiting | Forge Biologics, Inc | 9 | 2023-02-03 | 2025-11-20 |
| MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis Stem Cell Transplantation, IMD Preparative Regimen, Osteopetrosis Only Preparative Regimen - Mucopolysaccharidosis Disorders, Hurler Syndrome | Phase 2 | Active not recruiting | Masonic Cancer Center, University of Minnesota | 149 | 2014-07-10 | 2026-11-03 |
Sphingolipidoses (2) · Alpha-Methylacyl-CoA Racemase Deficiency (1) · Aspartylglucosaminuria (1) · Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Central Nervous System Diseases (1) · Demyelinating Diseases (1) · Fucosidosis (1) · Genetic Diseases, Inborn (1) · Hereditary Central Nervous System Demyelinating Diseases (1) · Hereditary Diffuse Leukoencephalopathy with Spheroids (1) · Leukodystrophy, Metachromatic (1) · Leukoencephalopathies (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Heredodegenerative Disorders, Nervous System (2) · Nutritional and Metabolic Diseases (2) · Abnormalities, Multiple (1) · Bone Diseases (1) · Bone Diseases, Developmental (1) · Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Carbohydrate Metabolism, Inborn Errors (1) · Central Nervous System Diseases (1) · Congenital Abnormalities (1) · Connective Tissue Diseases (1) · Demyelinating Diseases (1) · Digestive System Diseases (1)
Regimen B (1) · Stem Cell Transplantation (1)
Forge Biologics, Inc (1) · Masonic Cancer Center, University of Minnesota (1)
United States (2)