Leukodystrophy, Globoid Cell: Clinical Trials

1 trial for Leukodystrophy, Globoid Cell, newest first

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1 completed. 1 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 11Completed 1

Follow Leukodystrophy, Globoid Cell: new trials by email Literature Review of Leukodystrophy, Globoid Cell trials Research Report on Leukodystrophy, Globoid Cell

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Human Placental-Derived Stem Cell Transplantation
Human Placental Derived Stem Cell - Mucopolysaccharidosis I, Mucopolysaccharidosis VI
Phase 1CompletedNew York Medical College432013-04-012022-10-25

Narrower conditions

Adrenoleukodystrophy (1)  ·  Anemia, Aplastic (1)  ·  Anemia, Diamond-Blackfan (1)  ·  Fucosidosis (1)  ·  Gaucher Disease (1)  ·  Leukemia, Myeloid, Acute (1)  ·  Leukodystrophy, Metachromatic (1)  ·  Metabolism, Inborn Errors (1)  ·  Mucopolysaccharidosis I (1)  ·  Mucopolysaccharidosis VI (1)  ·  Myelodysplastic Syndromes (1)  ·  Neuronal Ceroid-Lipofuscinoses (1)  ·  Niemann-Pick Diseases (1)  ·  Precursor Cell Lymphoblastic Leukemia-Lymphoma (1)

Broader conditions

Adrenal Gland Diseases (1)  ·  Adrenal Insufficiency (1)  ·  Anemia (1)  ·  Anemia, Hypoplastic, Congenital (1)  ·  Bone Marrow Diseases (1)  ·  Bone Marrow Failure Disorders (1)  ·  Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Carbohydrate Metabolism, Inborn Errors (1)  ·  Central Nervous System Diseases (1)  ·  Cholesterol Ester Storage Disease (1)  ·  Congenital Bone Marrow Failure Syndromes (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Connective Tissue Diseases (1)

Sponsors

New York Medical College (1)

Countries

United States (1)

Top investigators

Mitchell S Cairo, MD (1)