Hypophosphatemia, Familial: Clinical Trials

5 trials for Hypophosphatemia, Familial, newest first

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3 completed, 2 unknown. 5 Phase 4.

By phase and status

PhaseTrialsStatus
Phase 45Completed 3, Unknown 2

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Trials (filtered) newest first · largest first

All 5 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Study to Assess the Safety, Pharmacokinetics and Efficacy of KRN23 in Pediatric Chinese Patients With XLH
KRN23 - X-linked Hypophosphatemia (XLH)
Phase 4CompletedKyowa Kirin Co., Ltd.282021-11-012024-07-09
Study to Assess the Safety, Pharmacokinetics and Efficacy of KRN23 in Adult Chinese Patients With XLH
KRN23 - X-linked Hypophosphatemia (XLH)
Phase 4CompletedKyowa Kirin Co., Ltd.182021-09-282024-07-09
Examining the Effect of Burosumab on Muscle Function
Burosumab Injection [Crysvita] - X-linked Hypophosphatemia
Phase 4CompletedYale University102019-11-132023-08-24
Burosumab in Children and Adolescents With X-linked Hypophosphatemia
Burosumab Injection - Rare Diseases, X-linked Hypophosphatemia
Phase 4UnknownBicetre Hospital572018-03-182020-06-05
Using Different Doses of Active Vitamin D Combined With Neutral Phosphate in Children With X-linked Hypophosphatemia
Calcitriol - X-linked Hypophosphatemia
Phase 4UnknownPeking Union Medical College Hospital1002017-01-012019-01-30

Narrower conditions

Familial Hypophosphatemic Rickets (5)  ·  Hyperparathyroidism (1)  ·  Rare Diseases (1)

Broader conditions

Avitaminosis (5)  ·  Bone Diseases (5)  ·  Bone Diseases, Metabolic (5)  ·  Calcium Metabolism Disorders (5)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (5)  ·  Deficiency Diseases (5)  ·  Female Urogenital Diseases (5)  ·  Female Urogenital Diseases and Pregnancy Complications (5)  ·  Genetic Diseases, Inborn (5)  ·  Hypophosphatemia (5)  ·  Kidney Diseases (5)  ·  Male Urogenital Diseases (5)  ·  Malnutrition (5)  ·  Metabolic Diseases (5)

Interventions

burosumab (4)  ·  Calcitriol (1)

Sponsors

Kyowa Kirin Co., Ltd. (2)  ·  Bicetre Hospital (1)  ·  Peking Union Medical College Hospital (1)  ·  Yale University (1)

Countries

China (3)  ·  France (1)  ·  United States (1)

Top investigators

Karl L Insogna, M.D. (1)